| 2/1/26 |
Pharming (PHAR) |
Joenja for Activated PI3K Delta Syndrome (APDS) |
Subscribers Only |
Subscribers Only |
Subscribers Only |
| 1/29/26 |
Delta-Fly (4598) |
DFP-10917 for Acute Myelogenous Leukemia (AML) |
Subscribers Only |
Subscribers Only |
Subscribers Only |
| 1/27/26 |
Sarepta Therapeutics (SRPT) |
Elevidys for Duchenne Muscular Dystrophy (DMD) |
Subscribers Only |
Subscribers Only |
Subscribers Only |
| 1/23/26 |
Trevi (TRVI) |
Haduvio for Chronic Cough |
Subscribers Only |
Subscribers Only |
Subscribers Only |
| 1/22/26 |
IntraBio |
Aqneursa for Ataxia Telangiectasia |
Subscribers Only |
Subscribers Only |
Subscribers Only |